PG
Paul Gissen
University College London, University of Birmingham, University of Glasgow
0000-0002-9712-6122
Employment
-
University College London Professor2011 - Present
-
University College London
Education
-
University of Birmingham PhD2002 - 2005
-
University of Glasgow MBCHB with Commendation1990 - 1995
Projects & Funding
Projects & funding information is unavailable.
Publications (488)
- Longitudinal outcomes of non-transplanted ornithine transcarbamylase deficiency in males and females: a multicentre UK natural history cohort Save
- Identification of AAV Vector Integration Sites in Primary Human and Macaque Hepatocytes in vivo, and Analysis of Oncogenic Risk. Save
- Safety and efficacy analysis of in vivo lentiviral gene therapy in pre-clinical ARC syndrome models. Save
- First-in-human clinical trial of AAV9-mediated gene augmentation therapy for CTNNB1 neurodevelopmental syndrome Save
- GLP-1 gene therapy normalises weight gain and improves glucose homeostasis in a mouse model of hypothalamic obesity Save
- Moving AAV9 gene therapy for Niemann-Pick type C1 disease towards the clinic Save
- 2025 Consensus Clinical Management Guidelines for Niemann-Pick Disease Type C Save
- The Evolving Landscape of Fetal Therapy: Surgical Interventions and Emerging Biologics Save
- Recommendations for the diagnosis and management of cln3 disease (batten disease) using the Delphi consensus methodology. Save
- Characterizing a Unique Retinal Phenotype in INTS11-Associated Neurodevelopmental Disorder. Save